US2006276489A1PendingUtilityA1

Inhibitors of Tubulin Polymerization

Assignee: RIGEL PHARMACEUTICALS INCPriority: Feb 15, 2002Filed: May 9, 2006Published: Dec 7, 2006
Est. expiryFeb 15, 2022(expired)· nominal 20-yr term from priority
C07D 495/04
56
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Claims

Abstract

The invention relates to the inhibition of tubulin polymerization. The invention provides compounds and methods for inhibiting tubulin polymerization. The invention also provides compositions and methods for treating cell proliferative diseases and conditions.

Claims

exact text as granted — not AI-modified
1 . A method of treating a patient with colon cancer, the method comprising administering to the patient an effective amount of a compound of the formula (1):  
     
       
         
         
             
             
         
       
       or a pharmaceutically acceptable salt thereof, alone or in combination with a pharmaceutically acceptable carrier, excipient, or diluent wherein  
       R 1  and R 2  are independently selected from the group consisting of —H, halo, C 1 -C 6  alkyl, halogenated-C 1 -C 6 -alkyl, and —OR 4 , or  
       R 1  and R 2  together with the carbon to which they are attached form a heterocyclyl;  
       R 4  is selected from the group consisting of C 1 -C 6  alkyl, or  
       R 4  is aryl or aryl-C 1 -C 6 -alkyl, wherein the aryl portion is optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —NR 5 R 6 , or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1  -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine;  
 
       R 5  and R 6  are each independently hydrogen, cyano, oxo, carboxamido, amidino, C 1 -C 8  hydroxyalkyl, C 1 -C 3  alkylaryl, aryl-C 1 -C 3  alkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, aryl-C 1 -C 3  alkoxycarbonyl, C 2 -C 8  acyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, aroyl, aryl, cycloalkyl, heterocyclyl, or heteroaryl, wherein each optionally substituted with one more groups selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidine, or  
       R 5  and R 6  taken together with the N to which they are attached form a heterocyclyl or heteroaryl, each of which is optionally substituted with from 1 to 3 substituents selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidine;  
       L is selected from the group consisting of a covalent bond, C 1 -C 6  alkyl, —C(O)—, and —(CH 2 ) 0-3 C(H)(R 5 )—;  
       R 5  is selected from the group consisting of C 1 -C 6  alkyl, aryl, aryl-C 1 -C 6 -alkyl, —R 6 —S—R 7 , —R 6 —C(O)OR 7 , and —R 6 —O—R 7 , wherein R 6  and R 7  are C 1 -C 6  alkyl;  
       R 3  is selected from the group consisting of H, C 1 -C 6  alkyl, hydroxy C 1 -C 6  alkyl, —OR 8 , —C(O)OR 9 , —N(R 10 )R 11 , or  
       R 3  is C 3 -C 8 -cycloalkyl, heterocyclyl, aryl, heteroaryl, arylalkyl, each of which is optionally substituted with one to four groups selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —NR 5 R 6 , or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine;  
 
       R 8  is C 1 -C 6  alkyl or hydroxy C 1 -C 6  alkyl; and  
       R 9  R 10 , and R 11  are C 1 -C 6  alkyl.  
     
   
   
       2 . The method of  claim 1  wherein R 2  is H.  
   
   
       3 . The method of  claim 1  wherein R 1  and R 2  are independently selected from the group consisting of H, halogen, C 1 -C 6  alkyl, and —OR 4 , wherein R 4  is C 1 -C 6  alkyl, or wherein R 1  and R 2  together with the carbon to which they are attached form a heterocyclyl moiety.  
   
   
       4 . The method of  claim 1  wherein R 1  and R 2  are independently selected from the group consisting of H, —Cl, —CH 3 , and —OCH 3 , or wherein R 1  and R 2  together with the carbon to which they are attached form a 5- or 6-membered heterocyclyl moiety.  
   
   
       5 . The method of  claim 1  wherein L is a covalent bond.  
   
   
       6 . The method of  claim 1  wherein L is C 1 -C 6  alkyl.  
   
   
       7 . The method of  claim 1  wherein L is —(CH 2 ) 0-1 C(H)(R 5 )—.  
   
   
       8 . The method of  claim 5  wherein 
 R 3  is selected from the group consisting of H, hydroxy alkyl, or    R 3  is cycloalkyl, heterocyclyl, aryl, or heteroaryl, each of which is optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —NR 30 R 31 , or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine.  
   
   
   
       9 . The method of  claim 8  wherein 
 R 3  is H, or    R 3  is C 3 -C 6  cycloalkyl, 5- to 6-membered heterocyclyl, or aryl, each of which is optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —NR 30 R 31 , or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine.  
   
   
   
       10 . The method of  claim 9  wherein 
 R 3  is selected from the group consisting of cyclopropyl, benzyl, or    R 3  is benzyl optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —NR 30 R 31 , or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine.  
   
   
   
       11 . The method of  claim 10  wherein R 3  is benzyl optionally substituted with one to three substituents independently selected from the group consisting of —CH 3 , —CO 2 H, —CO 2 CH 2 CH 3 , —OCH 3 , —CF 3 , —CN, —NO 2 , —SO 2 NH 2 , and —Cl.  
   
   
       12 . The method of  claim 6  wherein 
 R 3  is selected from the group consisting of H, —OR 8 , —C(O)OR 9 , and —N(R 10 )R 11 , or    R 3  is cycloalkyl, heterocyclyl, aryl or heteroaryl, each of which is optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —NR 30 R 31 R, or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine.  
   
   
   
       13 . The method of  claim 12  wherein 
 R 3  is selected from the group consisting of H, C 3 -C 6  cycloalkyl, 4- to 6-membered heterocyclyl, —OR 8 , or    R 3  is optionally benzyl, each of which is optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —N 30 R 31 R, or 
 C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine.  
   
   
   
       14 . The method of  claim 13  wherein 
 R 3  is H or —OCH 3 , or    R 3  is 5- to 6-membered heterocyclyl or benzyl, each of which is optionally substituted with one to four groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino, guanidino, —(CH 2 ) s —N 30 R 31 , or    C 1 -C 5  alkyl or alkenyl or arylalkyl imino, carbamoyl, azido, carboxamido, mercapto, hydroxy, hydroxyalkyl, alkylaryl, arylalkyl, C 1 -C 8  alkyl, C 1 -C 8  alkenyl, C 1 -C 8  alkoxy, C 1 -C 8  alkoxycarbonyl, aryloxycarbonyl, C 2 -C 8  acyl, C 2 -C 8  acylamino, C 1 -C 8  alkylthio, arylalkylthio, arylthio, C 1 -C 8  alkylsulfinyl, arylalkylsulfinyl, arylsulfinyl, C 1 -C 8  alkylsulfonyl, arylalkylsulfonyl, arylsulfonyl, C 0 -C 6  N-alkyl carbamoyl, C 2 -C 15  N,N-dialkylcarbamoyl, C 3 -C 7  cycloalkyl, aroyl, aryloxy, arylalkyl ether, aryl, aryl fused to a cycloalkyl or heterocycle or another aryl ring, C 3 -C 7  heterocycle, or any of these rings fused or spiro-fused to a cycloalkyl, heterocyclyl, or aryl, each of which is optionally substituted with one or more groups independently selected from halo, cyano, oxo, carboxy, formyl, nitro, amino, amidino or guanidine.    
   
   
       15 . The method of  claim 1  selected from the group consisting of:  
     
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
     
   
   
       16 . The method of  claim 15  selected from the group consisting of:  
     
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
     
   
   
       17 . The method of  claim 16  selected from the group consisting of:  
     
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
       
         
         
             
             
         
       
     
   
   
       18 . The method of  claim 17  selected from the group consisting of:

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