US2005277588A1PendingUtilityA1

Compounds having affinity for the granulocyte-colony stimulating factor receptor (G-CSFR) and associated uses

Individually held — no corporate assignee on recordPriority: Jul 20, 2000Filed: Aug 30, 2004Published: Dec 15, 2005
Est. expiryJul 20, 2020(expired)· nominal 20-yr term from priority
C07K 14/53A61K 38/00C07K 14/535
58
PatentIndex Score
0
Cited by
0
References
0
Claims

Abstract

Novel compounds are provided that bind to G-CSFR. The novel compounds have a peptide chain approximately 6 to 40 amino acids in length that binds to G-CSFR. The compounds are useful as probes for affinity screening. In addition, the compounds have demonstrated agonist or antagonist activity for the G-CSFR, and are therefore useful in treatment of diseases including patients who suffer from a low white blood cell titer. Pharmaceutical compositions and methods of use are provided as well.

Claims

exact text as granted — not AI-modified
1 . A compound comprising a peptide chain approximately 10 to 40 amino acids in length that binds to G-CSFR and contains a sequence of amino acids of formula (I) CX 1 X 2 X 3 X 4 X 5 X 6 X 7 X 8 C (SEQ ID NO: 1), wherein each amino acid is indicated by standard one-letter abbreviation, and wherein X 1  is A, N, S, F, D, G, L, T, E, V, P, Q, H, M or K; X 2  is M, G, R, H, D, I, V, A, S, E, N, F, Y, P, C, W or T; X 3  is E, V, W, F, M, A, N, S, L, T, Y, G or P; X 4  is V, I, G, Q, W, M, T, Y, L, P, D, C, E or A; X 5  is M, E, W, L, P, N, I, T, V, F, Y, Q, S, R, W, G, H or D; X 6  is H, A, W, Y, V, F, Q, M, N, E, S, D, P or G. X 7  is M, F, Y, V, N, L, H, D, S, W, G, Q, C or T; and X 8  is C, Y, R, I, K, W, L, E, M, H, A, T, F, D, P, G or Q:  
     
     
         2 . The compound of  claim 1  wherein X 1  is D or P.  
     
     
         3 . The compound of  claim 1  wherein X 2  is D or P.  
     
     
         4 . The ccmpound of  claim 1  wherein X 3  is E or W.  
     
     
         5 . The compound of  claim 1  wherein X 4  is V, I, or Y.  
     
     
         6 . The compound of  claim 1  wherein X 5  is M or L.  
     
     
         7 . The compound of  claim 1  wherein X 6  is W, Y or F.  
     
     
         8 . The compound of  claim 1  wherein X 7  is M, Y or D.  
     
     
         9 . The compound of  claim 1  wherein X 8  is C or M.  
     
     
         10 . The compound of  claim 1  that comprises a sequence selected from the following group:  
       
         
           
                 
                 
                 
                 
               
                     
                     
                 
                     
                   CNREIEAMCC; 
                   (SEQ ID NO: 9) 
                     
                 
                     
                     
                 
                     
                   CADEVMHFCC; 
                   (SEQ ID NO: 10) 
                 
                     
                     
                 
                     
                   CNREIMWMCC; 
                   (SEQ ID NO: 11) 
                 
                     
                     
                 
                     
                   CSHEVWWYCC; 
                   (SEQ ID NO: 12) 
                 
                     
                     
                 
                     
                   CSREVLYYCC; 
                   (SEQ ID NO: 13) 
                 
                     
                     
                 
                     
                   CFIEGPWVCC; 
                   (SEQ ID NO: 14) 
                 
                     
                     
                 
                     
                   CFVEGNWYCC; 
                   (SEQ ID NO: 15) 
                 
                     
                     
                 
                     
                   CAAEVMVNCC; 
                   (SEQ ID NO: 16) 
                 
                     
                     
                 
                     
                   CSDEVIFYCC; 
                   (SEQ ID NO: 17) 
                 
                     
                     
                 
                     
                   CDREIMWFCC; 
                   (SEQ ID NO: 18) 
                 
                     
                     
                 
                     
                   CAHEVMWMCC; 
                   (SEQ ID NO: 19) 
                 
                     
                     
                 
                     
                   CGSEVTFMCC; 
                   (SEQ ID NO: 20) 
                 
                     
                     
                 
                     
                   CLEEIMWLCC; 
                   (SEQ ID NO: 21) 
                 
                     
                     
                 
                     
                   CAREVLAMCC; 
                   (SEQ ID NO: 22) 
                 
                     
                     
                 
                     
                   CSVEVMQMCC; 
                   (SEQ ID NO: 23) 
                 
                     
                     
                 
                     
                   CTNVQLMHYC; 
                   (SEQ ID NO: 24) 
                 
                     
                     
                 
                     
                   CDVWQLFDRC; 
                   (SEQ ID NO: 25) 
                 
                     
                     
                 
                     
                   CSFVQLNSIC; 
                   (SEQ ID NO: 26) 
                 
                     
                     
                 
                     
                   CDYWQWFDKC; 
                   (SEQ ID NO: 27) 
                 
                     
                     
                 
                     
                   CESFWVELWC; 
                   (SEQ ID NO: 28) 
                 
                     
                     
                 
                     
                   CVPWMFYDLC; 
                   (SEQ ID NO: 29) 
                 
                     
                     
                 
                     
                   CDPWMFYDLC; 
                   (SEQ ID NO: 30) 
                 
                     
                     
                 
                     
                   CDPWVLFDEC; 
                   (SEQ ID NO: 31) 
                 
                     
                     
                 
                     
                   CDHWTYFDMC; 
                   (SEQ ID NO: 32) 
                 
                     
                     
                 
                     
                   CVVWTLYDKC; 
                   (SEQ ID NO: 33) 
                 
                     
                     
                 
                     
                   CPDWYQSYMC; 
                   (SEQ ID NO: 34) 
                 
                     
                     
                 
                     
                   CPDWYSYYMC; 
                   (SEQ ID NO: 35) 
                 
                     
                     
                 
                     
                   CPEWYTDVMC; 
                   (SEQ ID NO: 36) 
                 
                     
                     
                 
                     
                   CPDWYLDYMC; 
                   (SEQ ID NO: 37) 
                 
                     
                     
                 
                     
                   CPEWYLDYMC; 
                   (SEQ ID NO: 38) 
                 
                     
                     
                 
                     
                   CPDWYLPYMC; 
                   (SEQ ID NO: 39) 
                 
                     
                     
                 
                     
                   CPEWYLPYMC; 
                   (SEQ ID NO: 40) 
                 
                     
                     
                 
                     
                   CQDWWVELWC; 
                   (SEQ ID NO: 41) 
                 
                     
                     
                 
                     
                   CPDWYLPWMC; 
                   (SEQ ID NO: 42) 
                 
                     
                     
                 
                     
                   CACMLRVVHC; 
                   (SEQ ID NO: 43) 
                 
                     
                     
                 
                     
                   CQRAGYMLAC; 
                   (SEQ ID NO: 44) 
                 
                     
                     
                 
                     
                   CHANPVWGEC; 
                   (SEQ ID NO: 45) 
                 
                     
                     
                 
                     
                   CFWSDWGQTC; 
                   (SEQ ID NO: 46) 
                 
                     
                     
                 
                     
                   CPHWTSYYMC; 
                   (SEQ ID NO: 47) 
                 
                     
                     
                 
                     
                   CETLCGACFC; 
                   (SEQ ID NO: 48) 
                 
                     
                     
                 
                     
                   CATTINDTLC; 
                   (SEQ ID NO: 49) 
                 
                     
                     
                 
                     
                   CLNYPHPVFC; 
                   (SEQ ID NO: 50) 
                 
                     
                     
                 
                     
                   CMDGEMAVDC; 
                   (SEQ ID NO: 51) 
                 
                     
                     
                 
                     
                   CNMGWMSWPC 
                   (SEQ ID NO: 52) 
                 
                     
                     
                 
                     
                   CETYADWLGC; 
                   (SEQ ID NO: 53) 
                 
                     
                     
                 
                     
                   CDPWMFFDMC; 
                   (SEQ ID NO: 54) 
                 
                     
                     
                 
                     
                   CDPWIWYDLC; 
                   (SEQ ID NO: 55) 
                 
                     
                     
                 
                     
                   CDPWIMYDRC; 
                   (SEQ ID NO: 56) 
                 
                     
                     
                 
                     
                   CDPWVFFDIC; 
                   (SEQ ID NO: 57) 
                 
                     
                     
                 
                     
                   CDPWTYYDLC; 
                   (SEQ ID NO: 58) 
                 
                     
                     
                 
                     
                   CDPWIFYDRC; 
                   (SEQ ID NO: 59) 
                 
                     
                     
                 
                     
                   CDPWLFYDLC; 
                   (SEQ ID NO: 60) 
                 
                     
                     
                 
                     
                   CDPWVWYDLC; 
                   (SEQ ID NO: 61) 
                 
                     
                     
                 
                     
                   CDPWIFFDRC; 
                   (SEQ ID NO: 62) 
                 
                     
                     
                 
                     
                   CDPWMFFDQC; 
                   (SEQ ID NO: 63) 
                 
                     
                     
                 
                     
                   CDPWLWYDRC; 
                   (SEQ ID NO: 64) 
                 
                     
                     
                 
                     
                   CDVWVWYDQC; 
                   (SEQ ID NO: 65) 
                 
                     
                     
                 
                     
                   CDPWIYYDLC; 
                   (SEQ ID NO: 66) 
                 
                     
                     
                 
                     
                   CVPWTLFDLC; 
                   (SEQ ID NO: 67) 
                 
                     
                     
                 
                     
                   CPAWYLEYMC; 
                   (SEQ ID NO: 68) 
                 
                     
                     
                 
                     
                   CPDWYLEYMC; 
                   (SEQ ID NO: 69) 
                 
                     
                     
                 
                     
                   CKYWQWFDKC; 
                   (SEQ ID NO: 70) 
                 
                     
                     
                 
                     
                   CDHWMWYDKC. 
                   (SEQ ID NO: 71) 
                 
                     
                     
                 
                     
                   GCNREIEAMCCG; 
                   (SEQ ID NO: 72) 
                 
                     
                     
                 
                     
                   GCPEWYTDVMCG; 
                   (SEQ ID NO: 73) 
                 
                     
                     
                 
                     
                   NWYCMDGEMAVDCEAT; 
                   (SEQ ID NO: 74) 
                 
                     
                     
                 
                     
                   WQSCNMGWMSWPCYFV; 
                   (SEQ ID NO: 75) 
                 
                     
                     
                 
                     
                   HELCETYADWLGCVEW; 
                   (SEQ ID NO: 76) 
                 
                     
                     
                 
                     
                   PCDPWMFFDMCERW; 
                   (SEQ ID NO: 77) 
                 
                     
                     
                 
                     
                   LRGCDPWIWYDLCPAV; 
                   (SEQ ID NO: 78) 
                 
                     
                     
                 
                     
                   GYLCDPWIFYDRCLGF; 
                   (SEQ ID NO: 79) 
                 
                     
                     
                 
                     
                   RFACDPWVFFDICGYW; 
                   (SEQ ID NO: 80) 
                 
                     
                     
                 
                     
                   GYWCDPWTYYDLCLTA; 
                   (SEQ ID NO: 81) 
                 
                     
                     
                 
                     
                   MWTCDPWIFYDRCFLN; 
                   (SEQ ID NO: 82) 
                 
                     
                     
                 
                     
                   GSSCDPWLFYDLCLLD; 
                   (SEQ ID NO: 83) 
                 
                     
                     
                 
                     
                   GGGCDPWVWYDLCWCD; 
                   (SEQ ID NO: 84) 
                 
                     
                     
                 
                     
                   YTSCDPWIFFDRCMSV; 
                   (SEQ ID NO: 85) 
                 
                     
                     
                 
                     
                   DPYCDPWMFFDQCAYL; 
                   (SEQ ID NO: 86) 
                 
                     
                     
                 
                     
                   REFCDPWLWYDRCL; 
                   (SEQ ID NO: 87) 
                 
                     
                     
                 
                     
                   NTGCDVWVWYDQCFAM; 
                   (SEQ ID NO: 88) 
                 
                     
                     
                 
                     
                   LVFCDPWIYYDLCMDT; 
                   (SEQ ID NO: 89) 
                 
                     
                     
                 
                     
                   GCSFVQLNSICG; 
                   (SEQ ID NO: 90) 
                 
                     
                     
                 
                     
                   GCPAWYLEYMCG; 
                   (SEQ ID NO: 91) 
                 
                     
                     
                 
                     
                   GCPDWYLEYMCG; 
                   (SEQ ID NO: 92) 
                 
                     
                     
                 
                     
                   GCKYWQWFDKCG; 
                   (SEQ ID NO: 93) 
                 
                     
                   and 
                 
                     
                     
                 
                     
                   GCDHWMWYDKCG. 
                   (SEQ ID NO: 94) 
                 
                     
                     
                 
             
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
                
               
            
           
         
       
     
     
         11 . The compound of  claim 1 , containing a disulfide bond.  
     
     
         12 . The compound of claims  1  wherein the N terminus of the peptide is coupled to a polyethylene glycol molecule.  
     
     
         13 . The compound of  claim 1  wherein the N terminus of the peptide is acetylated.  
     
     
         14 . The compound of  claim 1 , wherein the C terminus of the peptide is amidated.  
     
     
         15 . The compound of  claim 1  having  
     
     
         16 . The compound of  claim 1  having structure:  
       
         
           
           
               
               
           
         
       
       wherein R 1  and R 2  are independently selected from the sequences of amino acids of formula (V); βA is a β-alanine residue; n1, n2, n3, n4, x and y are independently zero or one with the proviso that the sum of x and y is either one or two; and Lk is a terminal linking moiety selected from the group consisting of a disulfide bond, a carbonyl moiety, a C1-12 linking moiety optionally terminated with one or two-NH-linkages and optionally substituted at one or more available carbon atoms with a lower alkyl substituent, a lysine residue or a lysine amide.  
     
     
         17 . A pharmaceutical composition comprising a therapeutically effective amount of the compound of  claim 1 , in combination with a pharmaceutically acceptable carrier.  
     
     
         18 . A method for treating a patient who would benefit from administration of a GCSF modulator, comprising administering to the patient a therapeutically effective amount of a compound of  claim 1 .  
     
     
         19 . The method of  claim 16 , wherein the G-CSF modulator is an agonist for the GCSFR.  
     
     
         20 . The method of  claim 16 , wherein the patient suffers from a depressed neutrophil count.  
     
     
         21 . The method of  claim 18 , wherein the depressed neutrophil count is associated with a condition selected from the group consisting of chemotherapy-induced neutropenia, AIDS induced neutropenia and community-acquired pneumonia-induced neutropenia.

Join the waitlist — get patent alerts

Track US2005277588A1 — get alerts on status changes and closely related new filings.

We store only your email — no account needed. See our privacy policy.